1 Introduction to Research & Analysis Reports
1.1 Adenosine Deaminase Deficiency Treatment Market Definition
1.2 Market Segments
1.2.1 Market by Type
1.2.2 Market by Application
1.3 Global Adenosine Deaminase Deficiency Treatment Market Overview
1.4 Features & Benefits of This Report
1.5 Methodology & Sources of Information
1.5.1 Research Methodology
1.5.2 Research Process
1.5.3 Base Year
1.5.4 Report Assumptions & Caveats
2 Global Adenosine Deaminase Deficiency Treatment Overall Market Size
2.1 Global Adenosine Deaminase Deficiency Treatment Market Size: 2022 VS 2029
2.2 Global Adenosine Deaminase Deficiency Treatment Market Size, Prospects & Forecasts: 2018-2029
2.3 Key Market Trends, Opportunity, Drivers and Restraints
2.3.1 Market Opportunities & Trends
2.3.2 Market Drivers
2.3.3 Market Restraints
3 Company Landscape
3.1 Top Adenosine Deaminase Deficiency Treatment Players in Global Market
3.2 Top Global Adenosine Deaminase Deficiency Treatment Companies Ranked by Revenue
3.3 Global Adenosine Deaminase Deficiency Treatment Revenue by Companies
3.4 Top 3 and Top 5 Adenosine Deaminase Deficiency Treatment Companies in Global Market, by Revenue in 2022
3.5 Global Companies Adenosine Deaminase Deficiency Treatment Product Type
3.6 Tier 1, Tier 2 and Tier 3 Adenosine Deaminase Deficiency Treatment Players in Global Market
3.6.1 List of Global Tier 1 Adenosine Deaminase Deficiency Treatment Companies
3.6.2 List of Global Tier 2 and Tier 3 Adenosine Deaminase Deficiency Treatment Companies
4 Market Sights by Product
4.1 Overview
4.1.1 By Type – Global Adenosine Deaminase Deficiency Treatment Market Size Markets, 2022 & 2029
4.1.2 Adagen
4.1.3 Revcovi
4.2 By Type – Global Adenosine Deaminase Deficiency Treatment Revenue & Forecasts
4.2.1 By Type – Global Adenosine Deaminase Deficiency Treatment Revenue, 2018-2023
4.2.2 By Type – Global Adenosine Deaminase Deficiency Treatment Revenue, 2024-2029
4.2.3 By Type – Global Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
5 Sights by Application
5.1 Overview
5.1.1 By Application – Global Adenosine Deaminase Deficiency Treatment Market Size, 2022 & 2029
5.1.2 Hospital
5.1.3 Pharmacy
5.2 By Application – Global Adenosine Deaminase Deficiency Treatment Revenue & Forecasts
5.2.1 By Application – Global Adenosine Deaminase Deficiency Treatment Revenue, 2018-2023
5.2.2 By Application – Global Adenosine Deaminase Deficiency Treatment Revenue, 2024-2029
5.2.3 By Application – Global Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
6 Sights by Region
6.1 By Region – Global Adenosine Deaminase Deficiency Treatment Market Size, 2022 & 2029
6.2 By Region – Global Adenosine Deaminase Deficiency Treatment Revenue & Forecasts
6.2.1 By Region – Global Adenosine Deaminase Deficiency Treatment Revenue, 2018-2023
6.2.2 By Region – Global Adenosine Deaminase Deficiency Treatment Revenue, 2024-2029
6.2.3 By Region – Global Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
6.3 North America
6.3.1 By Country – North America Adenosine Deaminase Deficiency Treatment Revenue, 2018-2029
6.3.2 US Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.3.3 Canada Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.3.4 Mexico Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.4 Europe
6.4.1 By Country – Europe Adenosine Deaminase Deficiency Treatment Revenue, 2018-2029
6.4.2 Germany Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.4.3 France Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.4.4 U.K. Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.4.5 Italy Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.4.6 Russia Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.4.7 Nordic Countries Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.4.8 Benelux Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.5 Asia
6.5.1 By Region – Asia Adenosine Deaminase Deficiency Treatment Revenue, 2018-2029
6.5.2 China Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.5.3 Japan Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.5.4 South Korea Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.5.5 Southeast Asia Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.5.6 India Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.6 South America
6.6.1 By Country – South America Adenosine Deaminase Deficiency Treatment Revenue, 2018-2029
6.6.2 Brazil Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.6.3 Argentina Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.7 Middle East & Africa
6.7.1 By Country – Middle East & Africa Adenosine Deaminase Deficiency Treatment Revenue, 2018-2029
6.7.2 Turkey Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.7.3 Israel Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.7.4 Saudi Arabia Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
6.7.5 UAE Adenosine Deaminase Deficiency Treatment Market Size, 2018-2029
7 Adenosine Deaminase Deficiency Treatment Companies Profiles
7.1 Leadiant Biosciences
7.1.1 Leadiant Biosciences Company Summary
7.1.2 Leadiant Biosciences Business Overview
7.1.3 Leadiant Biosciences Adenosine Deaminase Deficiency Treatment Major Product Offerings
7.1.4 Leadiant Biosciences Adenosine Deaminase Deficiency Treatment Revenue in Global Market (2018-2023)
7.1.5 Leadiant Biosciences Key News & Latest Developments
8 Conclusion
9 Appendix
9.1 Note
9.2 Examples of Clients
9.3 Disclaimer
Table 1. Adenosine Deaminase Deficiency Treatment Market Opportunities & Trends in Global Market
Table 2. Adenosine Deaminase Deficiency Treatment Market Drivers in Global Market
Table 3. Adenosine Deaminase Deficiency Treatment Market Restraints in Global Market
Table 4. Key Players of Adenosine Deaminase Deficiency Treatment in Global Market
Table 5. Top Adenosine Deaminase Deficiency Treatment Players in Global Market, Ranking by Revenue (2022)
Table 6. Global Adenosine Deaminase Deficiency Treatment Revenue by Companies, (US$, Mn), 2018-2023
Table 7. Global Adenosine Deaminase Deficiency Treatment Revenue Share by Companies, 2018-2023
Table 8. Global Companies Adenosine Deaminase Deficiency Treatment Product Type
Table 9. List of Global Tier 1 Adenosine Deaminase Deficiency Treatment Companies, Revenue (US$, Mn) in 2022 and Market Share
Table 10. List of Global Tier 2 and Tier 3 Adenosine Deaminase Deficiency Treatment Companies, Revenue (US$, Mn) in 2022 and Market Share
Table 11. By Type – Global Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2022 & 2029
Table 12. By Type - Adenosine Deaminase Deficiency Treatment Revenue in Global (US$, Mn), 2018-2023
Table 13. By Type - Adenosine Deaminase Deficiency Treatment Revenue in Global (US$, Mn), 2024-2029
Table 14. By Application – Global Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2022 & 2029
Table 15. By Application - Adenosine Deaminase Deficiency Treatment Revenue in Global (US$, Mn), 2018-2023
Table 16. By Application - Adenosine Deaminase Deficiency Treatment Revenue in Global (US$, Mn), 2024-2029
Table 17. By Region – Global Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2022 & 2029
Table 18. By Region - Global Adenosine Deaminase Deficiency Treatment Revenue (US$, Mn), 2018-2023
Table 19. By Region - Global Adenosine Deaminase Deficiency Treatment Revenue (US$, Mn), 2024-2029
Table 20. By Country - North America Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2023
Table 21. By Country - North America Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2024-2029
Table 22. By Country - Europe Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2023
Table 23. By Country - Europe Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2024-2029
Table 24. By Region - Asia Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2023
Table 25. By Region - Asia Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2024-2029
Table 26. By Country - South America Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2023
Table 27. By Country - South America Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2024-2029
Table 28. By Country - Middle East & Africa Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2023
Table 29. By Country - Middle East & Africa Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2024-2029
Table 30. Leadiant Biosciences Company Summary
Table 31. Leadiant Biosciences Adenosine Deaminase Deficiency Treatment Product Offerings
Table 32. Leadiant Biosciences Adenosine Deaminase Deficiency Treatment Revenue (US$, Mn) & (2018-2023)
Table 33. Leadiant Biosciences Key News & Latest Developments
List of Figures
Figure 1. Adenosine Deaminase Deficiency Treatment Segment by Type in 2022
Figure 2. Adenosine Deaminase Deficiency Treatment Segment by Application in 2022
Figure 3. Global Adenosine Deaminase Deficiency Treatment Market Overview: 2022
Figure 4. Key Caveats
Figure 5. Global Adenosine Deaminase Deficiency Treatment Market Size: 2022 VS 2029 (US$, Mn)
Figure 6. Global Adenosine Deaminase Deficiency Treatment Revenue, 2018-2029 (US$, Mn)
Figure 7. The Top 3 and 5 Players Market Share by Adenosine Deaminase Deficiency Treatment Revenue in 2022
Figure 8. By Type - Global Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 9. By Application - Global Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 10. By Type - Global Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2022 & 2029
Figure 11. By Type - Global Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 12. By Application - Global Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2022 & 2029
Figure 13. By Application - Global Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 14. By Region - Global Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 15. By Country - North America Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 16. US Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 17. Canada Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 18. Mexico Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 19. By Country - Europe Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 20. Germany Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 21. France Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 22. U.K. Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 23. Italy Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 24. Russia Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 25. Nordic Countries Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 26. Benelux Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 27. By Region - Asia Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 28. China Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 29. Japan Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 30. South Korea Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 31. Southeast Asia Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 32. India Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 33. By Country - South America Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 34. Brazil Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 35. Argentina Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 36. By Country - Middle East & Africa Adenosine Deaminase Deficiency Treatment Revenue Market Share, 2018-2029
Figure 37. Turkey Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 38. Israel Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 39. Saudi Arabia Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 40. UAE Adenosine Deaminase Deficiency Treatment Revenue, (US$, Mn), 2018-2029
Figure 41. Leadiant Biosciences Adenosine Deaminase Deficiency Treatment Revenue Year Over Year Growth (US$, Mn) & (2018-2023)
※参考情報 アデノシンデアミナーゼ欠損症は、遺伝性の代謝異常の一つで、主に免疫システムに深刻な影響を与える疾患です。この疾患は、アデノシンデアミナーゼ(ADA)という酵素が欠乏していることによって引き起こされます。ADAは、アデノシンという核酸の前駆体を分解し、細胞内のアデノシン濃度を調節する役割を果たしています。この酵素が不足していると、アデノシンが高濃度になり、免疫細胞の機能が阻害され、重篤な免疫不全を引き起こします。 この障害は常染色体劣性遺伝で、両親からそれぞれの変異遺伝子を受け継ぐことで発症します。その結果、患者はウイルス感染や細菌感染に対して非常に脆弱な状態になります。特に幼少期に発症すると、重篤な感染症を引き起こし、早期に発見されて治療が行われなければ、生命に危険を及ぼすことがあります。 アデノシンデアミナーゼ欠損症の症状は、ほとんどの場合、出生時または幼少期に現れます。具体的には、慢性的な下痢、皮膚感染、肺炎、真菌感染など、多岐にわたる感染症の発症が見られます。また、免疫系が弱いため、予防接種後の副反応にも注意が必要です。特に生ワクチンに対する反応が問題視されることがあります。 治療方法としては、いくつかの選択肢があります。主な治療法は、骨髄移植や遺伝子治療です。骨髄移植は、ADAを正常に産生できるドナーからの細胞を移植することで、患者の免疫系を再構築する方法です。この治療法は特に幼少期の患者において有効であり、適切なマッチのドナーを見つけることが成功の鍵となります。しかし、この手技はリスクを伴うため、慎重に考慮する必要があります。 近年では、遺伝子治療も注目されています。遺伝子治療は、患者の細胞に正常なADA遺伝子を導入することで、ADAの産生を回復させ、免疫機能を改善する手法です。このアプローチにより、外部からの酵素投与に頼らずに、患者自身がADAを生産できるようになり、長期的な治療効果が期待されています。 さらに、治療には補助療法として酵素補充療法もあります。これは、欠損しているADAを体外から補充する方法で、投与されたADAが体内に取り込まれ、アデノシンの解毒を助ける仕組みです。しかし、効果を持続させるためには定期的な投与が必要であり、完全な治癒をもたらすものではありません。 アデノシンデアミナーゼ欠損症に関連する研究は、免疫学や遺伝学、細胞生物学などの分野で広がっています。新たな治療法の開発に向けた取り組みが進められており、特に遺伝子編集技術(CRISPR-Cas9など)の活用が期待されています。これにより、直ちに異常遺伝子を修正することができ、治療がより迅速に行える可能性があります。 また、患者の生活の質を改善するための支援体制も重要です。医療機関や専門家が連携して、患者とその家族に対する情報提供やサポートを行うことが求められます。症状や治療についての理解を深め、社会的なつながりを持つことで、患者の心理的な健康を維持する助けにもなるでしょう。 アデノシンデアミナーゼ欠損症の治療に関する課題はいくつか存在します。まず、早期診断が非常に重要です。新生児スクリーニングプログラムを介して、早期にこの疾患を発見することができるようになれば、将来的な治療の効果を大きく向上させることができます。また、社会的な認知度を高め、適切な治療を受けるための環境を整えることも重要です。 総じて、アデノシンデアミナーゼ欠損症は、治療法が進化しているものの、依然として多くの課題を抱えた疾患です。患者の生活の質を向上させるためには、医療従事者、研究者、患者、そしてその家族が協力し合い、最新の知見を共有し続けることが不可欠です。これからの研究と治療の進展によって、アデノシンデアミナーゼ欠損症の患者がより健康で充実した生活を送れることを期待しています。 |
❖ 免責事項 ❖
http://www.globalresearch.jp/disclaimer