1 Introduction to Research & Analysis Reports
1.1 Primary Hyperoxaluria Drug Market Definition
1.2 Market Segments
1.2.1 Market by Type
1.2.2 Market by Application
1.3 Global Primary Hyperoxaluria Drug Market Overview
1.4 Features & Benefits of This Report
1.5 Methodology & Sources of Information
1.5.1 Research Methodology
1.5.2 Research Process
1.5.3 Base Year
1.5.4 Report Assumptions & Caveats
2 Global Primary Hyperoxaluria Drug Overall Market Size
2.1 Global Primary Hyperoxaluria Drug Market Size: 2022 VS 2029
2.2 Global Primary Hyperoxaluria Drug Revenue, Prospects & Forecasts: 2018-2029
2.3 Global Primary Hyperoxaluria Drug Sales: 2018-2029
3 Company Landscape
3.1 Top Primary Hyperoxaluria Drug Players in Global Market
3.2 Top Global Primary Hyperoxaluria Drug Companies Ranked by Revenue
3.3 Global Primary Hyperoxaluria Drug Revenue by Companies
3.4 Global Primary Hyperoxaluria Drug Sales by Companies
3.5 Global Primary Hyperoxaluria Drug Price by Manufacturer (2018-2023)
3.6 Top 3 and Top 5 Primary Hyperoxaluria Drug Companies in Global Market, by Revenue in 2022
3.7 Global Manufacturers Primary Hyperoxaluria Drug Product Type
3.8 Tier 1, Tier 2 and Tier 3 Primary Hyperoxaluria Drug Players in Global Market
3.8.1 List of Global Tier 1 Primary Hyperoxaluria Drug Companies
3.8.2 List of Global Tier 2 and Tier 3 Primary Hyperoxaluria Drug Companies
4 Sights by Product
4.1 Overview
4.1.1 By Type – Global Primary Hyperoxaluria Drug Market Size Markets, 2022 & 2029
4.1.2 ALLN-230
4.1.3 DCR-PHXC
4.1.4 ALN-GO1
4.1.5 Others
4.2 By Type – Global Primary Hyperoxaluria Drug Revenue & Forecasts
4.2.1 By Type – Global Primary Hyperoxaluria Drug Revenue, 2018-2023
4.2.2 By Type – Global Primary Hyperoxaluria Drug Revenue, 2024-2029
4.2.3 By Type – Global Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
4.3 By Type – Global Primary Hyperoxaluria Drug Sales & Forecasts
4.3.1 By Type – Global Primary Hyperoxaluria Drug Sales, 2018-2023
4.3.2 By Type – Global Primary Hyperoxaluria Drug Sales, 2024-2029
4.3.3 By Type – Global Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
4.4 By Type – Global Primary Hyperoxaluria Drug Price (Manufacturers Selling Prices), 2018-2029
5 Sights by Application
5.1 Overview
5.1.1 By Application – Global Primary Hyperoxaluria Drug Market Size, 2022 & 2029
5.1.2 Hospital
5.1.3 Clinic
5.1.4 Others
5.2 By Application – Global Primary Hyperoxaluria Drug Revenue & Forecasts
5.2.1 By Application – Global Primary Hyperoxaluria Drug Revenue, 2018-2023
5.2.2 By Application – Global Primary Hyperoxaluria Drug Revenue, 2024-2029
5.2.3 By Application – Global Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
5.3 By Application – Global Primary Hyperoxaluria Drug Sales & Forecasts
5.3.1 By Application – Global Primary Hyperoxaluria Drug Sales, 2018-2023
5.3.2 By Application – Global Primary Hyperoxaluria Drug Sales, 2024-2029
5.3.3 By Application – Global Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
5.4 By Application – Global Primary Hyperoxaluria Drug Price (Manufacturers Selling Prices), 2018-2029
6 Sights by Region
6.1 By Region – Global Primary Hyperoxaluria Drug Market Size, 2022 & 2029
6.2 By Region – Global Primary Hyperoxaluria Drug Revenue & Forecasts
6.2.1 By Region – Global Primary Hyperoxaluria Drug Revenue, 2018-2023
6.2.2 By Region – Global Primary Hyperoxaluria Drug Revenue, 2024-2029
6.2.3 By Region – Global Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
6.3 By Region – Global Primary Hyperoxaluria Drug Sales & Forecasts
6.3.1 By Region – Global Primary Hyperoxaluria Drug Sales, 2018-2023
6.3.2 By Region – Global Primary Hyperoxaluria Drug Sales, 2024-2029
6.3.3 By Region – Global Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
6.4 North America
6.4.1 By Country – North America Primary Hyperoxaluria Drug Revenue, 2018-2029
6.4.2 By Country – North America Primary Hyperoxaluria Drug Sales, 2018-2029
6.4.3 US Primary Hyperoxaluria Drug Market Size, 2018-2029
6.4.4 Canada Primary Hyperoxaluria Drug Market Size, 2018-2029
6.4.5 Mexico Primary Hyperoxaluria Drug Market Size, 2018-2029
6.5 Europe
6.5.1 By Country – Europe Primary Hyperoxaluria Drug Revenue, 2018-2029
6.5.2 By Country – Europe Primary Hyperoxaluria Drug Sales, 2018-2029
6.5.3 Germany Primary Hyperoxaluria Drug Market Size, 2018-2029
6.5.4 France Primary Hyperoxaluria Drug Market Size, 2018-2029
6.5.5 U.K. Primary Hyperoxaluria Drug Market Size, 2018-2029
6.5.6 Italy Primary Hyperoxaluria Drug Market Size, 2018-2029
6.5.7 Russia Primary Hyperoxaluria Drug Market Size, 2018-2029
6.5.8 Nordic Countries Primary Hyperoxaluria Drug Market Size, 2018-2029
6.5.9 Benelux Primary Hyperoxaluria Drug Market Size, 2018-2029
6.6 Asia
6.6.1 By Region – Asia Primary Hyperoxaluria Drug Revenue, 2018-2029
6.6.2 By Region – Asia Primary Hyperoxaluria Drug Sales, 2018-2029
6.6.3 China Primary Hyperoxaluria Drug Market Size, 2018-2029
6.6.4 Japan Primary Hyperoxaluria Drug Market Size, 2018-2029
6.6.5 South Korea Primary Hyperoxaluria Drug Market Size, 2018-2029
6.6.6 Southeast Asia Primary Hyperoxaluria Drug Market Size, 2018-2029
6.6.7 India Primary Hyperoxaluria Drug Market Size, 2018-2029
6.7 South America
6.7.1 By Country – South America Primary Hyperoxaluria Drug Revenue, 2018-2029
6.7.2 By Country – South America Primary Hyperoxaluria Drug Sales, 2018-2029
6.7.3 Brazil Primary Hyperoxaluria Drug Market Size, 2018-2029
6.7.4 Argentina Primary Hyperoxaluria Drug Market Size, 2018-2029
6.8 Middle East & Africa
6.8.1 By Country – Middle East & Africa Primary Hyperoxaluria Drug Revenue, 2018-2029
6.8.2 By Country – Middle East & Africa Primary Hyperoxaluria Drug Sales, 2018-2029
6.8.3 Turkey Primary Hyperoxaluria Drug Market Size, 2018-2029
6.8.4 Israel Primary Hyperoxaluria Drug Market Size, 2018-2029
6.8.5 Saudi Arabia Primary Hyperoxaluria Drug Market Size, 2018-2029
6.8.6 UAE Primary Hyperoxaluria Drug Market Size, 2018-2029
7 Manufacturers & Brands Profiles
7.1 Allena Pharmaceuticals Inc
7.1.1 Allena Pharmaceuticals Inc Company Summary
7.1.2 Allena Pharmaceuticals Inc Business Overview
7.1.3 Allena Pharmaceuticals Inc Primary Hyperoxaluria Drug Major Product Offerings
7.1.4 Allena Pharmaceuticals Inc Primary Hyperoxaluria Drug Sales and Revenue in Global (2018-2023)
7.1.5 Allena Pharmaceuticals Inc Key News & Latest Developments
7.2 Alnylam Pharmaceuticals Inc
7.2.1 Alnylam Pharmaceuticals Inc Company Summary
7.2.2 Alnylam Pharmaceuticals Inc Business Overview
7.2.3 Alnylam Pharmaceuticals Inc Primary Hyperoxaluria Drug Major Product Offerings
7.2.4 Alnylam Pharmaceuticals Inc Primary Hyperoxaluria Drug Sales and Revenue in Global (2018-2023)
7.2.5 Alnylam Pharmaceuticals Inc Key News & Latest Developments
7.3 Dicerna Pharmaceuticals Inc
7.3.1 Dicerna Pharmaceuticals Inc Company Summary
7.3.2 Dicerna Pharmaceuticals Inc Business Overview
7.3.3 Dicerna Pharmaceuticals Inc Primary Hyperoxaluria Drug Major Product Offerings
7.3.4 Dicerna Pharmaceuticals Inc Primary Hyperoxaluria Drug Sales and Revenue in Global (2018-2023)
7.3.5 Dicerna Pharmaceuticals Inc Key News & Latest Developments
7.4 Intellia Therapeutics Inc
7.4.1 Intellia Therapeutics Inc Company Summary
7.4.2 Intellia Therapeutics Inc Business Overview
7.4.3 Intellia Therapeutics Inc Primary Hyperoxaluria Drug Major Product Offerings
7.4.4 Intellia Therapeutics Inc Primary Hyperoxaluria Drug Sales and Revenue in Global (2018-2023)
7.4.5 Intellia Therapeutics Inc Key News & Latest Developments
7.5 OxThera AB
7.5.1 OxThera AB Company Summary
7.5.2 OxThera AB Business Overview
7.5.3 OxThera AB Primary Hyperoxaluria Drug Major Product Offerings
7.5.4 OxThera AB Primary Hyperoxaluria Drug Sales and Revenue in Global (2018-2023)
7.5.5 OxThera AB Key News & Latest Developments
8 Global Primary Hyperoxaluria Drug Production Capacity, Analysis
8.1 Global Primary Hyperoxaluria Drug Production Capacity, 2018-2029
8.2 Primary Hyperoxaluria Drug Production Capacity of Key Manufacturers in Global Market
8.3 Global Primary Hyperoxaluria Drug Production by Region
9 Key Market Trends, Opportunity, Drivers and Restraints
9.1 Market Opportunities & Trends
9.2 Market Drivers
9.3 Market Restraints
10 Primary Hyperoxaluria Drug Supply Chain Analysis
10.1 Primary Hyperoxaluria Drug Industry Value Chain
10.2 Primary Hyperoxaluria Drug Upstream Market
10.3 Primary Hyperoxaluria Drug Downstream and Clients
10.4 Marketing Channels Analysis
10.4.1 Marketing Channels
10.4.2 Primary Hyperoxaluria Drug Distributors and Sales Agents in Global
11 Conclusion
12 Appendix
12.1 Note
12.2 Examples of Clients
12.3 Disclaimer
Table 1. Key Players of Primary Hyperoxaluria Drug in Global Market
Table 2. Top Primary Hyperoxaluria Drug Players in Global Market, Ranking by Revenue (2022)
Table 3. Global Primary Hyperoxaluria Drug Revenue by Companies, (US$, Mn), 2018-2023
Table 4. Global Primary Hyperoxaluria Drug Revenue Share by Companies, 2018-2023
Table 5. Global Primary Hyperoxaluria Drug Sales by Companies, (K Pcs), 2018-2023
Table 6. Global Primary Hyperoxaluria Drug Sales Share by Companies, 2018-2023
Table 7. Key Manufacturers Primary Hyperoxaluria Drug Price (2018-2023) & (USD/Pcs)
Table 8. Global Manufacturers Primary Hyperoxaluria Drug Product Type
Table 9. List of Global Tier 1 Primary Hyperoxaluria Drug Companies, Revenue (US$, Mn) in 2022 and Market Share
Table 10. List of Global Tier 2 and Tier 3 Primary Hyperoxaluria Drug Companies, Revenue (US$, Mn) in 2022 and Market Share
Table 11. By Type – Global Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2022 & 2029
Table 12. By Type - Global Primary Hyperoxaluria Drug Revenue (US$, Mn), 2018-2023
Table 13. By Type - Global Primary Hyperoxaluria Drug Revenue (US$, Mn), 2024-2029
Table 14. By Type - Global Primary Hyperoxaluria Drug Sales (K Pcs), 2018-2023
Table 15. By Type - Global Primary Hyperoxaluria Drug Sales (K Pcs), 2024-2029
Table 16. By Application – Global Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2022 & 2029
Table 17. By Application - Global Primary Hyperoxaluria Drug Revenue (US$, Mn), 2018-2023
Table 18. By Application - Global Primary Hyperoxaluria Drug Revenue (US$, Mn), 2024-2029
Table 19. By Application - Global Primary Hyperoxaluria Drug Sales (K Pcs), 2018-2023
Table 20. By Application - Global Primary Hyperoxaluria Drug Sales (K Pcs), 2024-2029
Table 21. By Region – Global Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2022 VS 2029
Table 22. By Region - Global Primary Hyperoxaluria Drug Revenue (US$, Mn), 2018-2023
Table 23. By Region - Global Primary Hyperoxaluria Drug Revenue (US$, Mn), 2024-2029
Table 24. By Region - Global Primary Hyperoxaluria Drug Sales (K Pcs), 2018-2023
Table 25. By Region - Global Primary Hyperoxaluria Drug Sales (K Pcs), 2024-2029
Table 26. By Country - North America Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2023
Table 27. By Country - North America Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2024-2029
Table 28. By Country - North America Primary Hyperoxaluria Drug Sales, (K Pcs), 2018-2023
Table 29. By Country - North America Primary Hyperoxaluria Drug Sales, (K Pcs), 2024-2029
Table 30. By Country - Europe Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2023
Table 31. By Country - Europe Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2024-2029
Table 32. By Country - Europe Primary Hyperoxaluria Drug Sales, (K Pcs), 2018-2023
Table 33. By Country - Europe Primary Hyperoxaluria Drug Sales, (K Pcs), 2024-2029
Table 34. By Region - Asia Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2023
Table 35. By Region - Asia Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2024-2029
Table 36. By Region - Asia Primary Hyperoxaluria Drug Sales, (K Pcs), 2018-2023
Table 37. By Region - Asia Primary Hyperoxaluria Drug Sales, (K Pcs), 2024-2029
Table 38. By Country - South America Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2023
Table 39. By Country - South America Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2024-2029
Table 40. By Country - South America Primary Hyperoxaluria Drug Sales, (K Pcs), 2018-2023
Table 41. By Country - South America Primary Hyperoxaluria Drug Sales, (K Pcs), 2024-2029
Table 42. By Country - Middle East & Africa Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2023
Table 43. By Country - Middle East & Africa Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2024-2029
Table 44. By Country - Middle East & Africa Primary Hyperoxaluria Drug Sales, (K Pcs), 2018-2023
Table 45. By Country - Middle East & Africa Primary Hyperoxaluria Drug Sales, (K Pcs), 2024-2029
Table 46. Allena Pharmaceuticals Inc Company Summary
Table 47. Allena Pharmaceuticals Inc Primary Hyperoxaluria Drug Product Offerings
Table 48. Allena Pharmaceuticals Inc Primary Hyperoxaluria Drug Sales (K Pcs), Revenue (US$, Mn) and Average Price (USD/Pcs) (2018-2023)
Table 49. Allena Pharmaceuticals Inc Key News & Latest Developments
Table 50. Alnylam Pharmaceuticals Inc Company Summary
Table 51. Alnylam Pharmaceuticals Inc Primary Hyperoxaluria Drug Product Offerings
Table 52. Alnylam Pharmaceuticals Inc Primary Hyperoxaluria Drug Sales (K Pcs), Revenue (US$, Mn) and Average Price (USD/Pcs) (2018-2023)
Table 53. Alnylam Pharmaceuticals Inc Key News & Latest Developments
Table 54. Dicerna Pharmaceuticals Inc Company Summary
Table 55. Dicerna Pharmaceuticals Inc Primary Hyperoxaluria Drug Product Offerings
Table 56. Dicerna Pharmaceuticals Inc Primary Hyperoxaluria Drug Sales (K Pcs), Revenue (US$, Mn) and Average Price (USD/Pcs) (2018-2023)
Table 57. Dicerna Pharmaceuticals Inc Key News & Latest Developments
Table 58. Intellia Therapeutics Inc Company Summary
Table 59. Intellia Therapeutics Inc Primary Hyperoxaluria Drug Product Offerings
Table 60. Intellia Therapeutics Inc Primary Hyperoxaluria Drug Sales (K Pcs), Revenue (US$, Mn) and Average Price (USD/Pcs) (2018-2023)
Table 61. Intellia Therapeutics Inc Key News & Latest Developments
Table 62. OxThera AB Company Summary
Table 63. OxThera AB Primary Hyperoxaluria Drug Product Offerings
Table 64. OxThera AB Primary Hyperoxaluria Drug Sales (K Pcs), Revenue (US$, Mn) and Average Price (USD/Pcs) (2018-2023)
Table 65. OxThera AB Key News & Latest Developments
Table 66. Primary Hyperoxaluria Drug Production Capacity (K Pcs) of Key Manufacturers in Global Market, 2021-2023 (K Pcs)
Table 67. Global Primary Hyperoxaluria Drug Capacity Market Share of Key Manufacturers, 2021-2023
Table 68. Global Primary Hyperoxaluria Drug Production by Region, 2018-2023 (K Pcs)
Table 69. Global Primary Hyperoxaluria Drug Production by Region, 2024-2029 (K Pcs)
Table 70. Primary Hyperoxaluria Drug Market Opportunities & Trends in Global Market
Table 71. Primary Hyperoxaluria Drug Market Drivers in Global Market
Table 72. Primary Hyperoxaluria Drug Market Restraints in Global Market
Table 73. Primary Hyperoxaluria Drug Raw Materials
Table 74. Primary Hyperoxaluria Drug Raw Materials Suppliers in Global Market
Table 75. Typical Primary Hyperoxaluria Drug Downstream
Table 76. Primary Hyperoxaluria Drug Downstream Clients in Global Market
Table 77. Primary Hyperoxaluria Drug Distributors and Sales Agents in Global Market
List of Figures
Figure 1. Primary Hyperoxaluria Drug Segment by Type in 2022
Figure 2. Primary Hyperoxaluria Drug Segment by Application in 2022
Figure 3. Global Primary Hyperoxaluria Drug Market Overview: 2022
Figure 4. Key Caveats
Figure 5. Global Primary Hyperoxaluria Drug Market Size: 2022 VS 2029 (US$, Mn)
Figure 6. Global Primary Hyperoxaluria Drug Revenue, 2018-2029 (US$, Mn)
Figure 7. Primary Hyperoxaluria Drug Sales in Global Market: 2018-2029 (K Pcs)
Figure 8. The Top 3 and 5 Players Market Share by Primary Hyperoxaluria Drug Revenue in 2022
Figure 9. By Type - Global Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2022 & 2029
Figure 10. By Type - Global Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
Figure 11. By Type - Global Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
Figure 12. By Type - Global Primary Hyperoxaluria Drug Price (USD/Pcs), 2018-2029
Figure 13. By Application - Global Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2022 & 2029
Figure 14. By Application - Global Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
Figure 15. By Application - Global Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
Figure 16. By Application - Global Primary Hyperoxaluria Drug Price (USD/Pcs), 2018-2029
Figure 17. By Region - Global Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2022 & 2029
Figure 18. By Region - Global Primary Hyperoxaluria Drug Revenue Market Share, 2018 VS 2022 VS 2029
Figure 19. By Region - Global Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
Figure 20. By Region - Global Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
Figure 21. By Country - North America Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
Figure 22. By Country - North America Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
Figure 23. US Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 24. Canada Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 25. Mexico Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 26. By Country - Europe Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
Figure 27. By Country - Europe Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
Figure 28. Germany Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 29. France Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 30. U.K. Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 31. Italy Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 32. Russia Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 33. Nordic Countries Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 34. Benelux Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 35. By Region - Asia Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
Figure 36. By Region - Asia Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
Figure 37. China Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 38. Japan Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 39. South Korea Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 40. Southeast Asia Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 41. India Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 42. By Country - South America Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
Figure 43. By Country - South America Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
Figure 44. Brazil Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 45. Argentina Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 46. By Country - Middle East & Africa Primary Hyperoxaluria Drug Revenue Market Share, 2018-2029
Figure 47. By Country - Middle East & Africa Primary Hyperoxaluria Drug Sales Market Share, 2018-2029
Figure 48. Turkey Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 49. Israel Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 50. Saudi Arabia Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 51. UAE Primary Hyperoxaluria Drug Revenue, (US$, Mn), 2018-2029
Figure 52. Global Primary Hyperoxaluria Drug Production Capacity (K Pcs), 2018-2029
Figure 53. The Percentage of Production Primary Hyperoxaluria Drug by Region, 2022 VS 2029
Figure 54. Primary Hyperoxaluria Drug Industry Value Chain
Figure 55. Marketing Channels
※参考情報 高シュウ酸尿症(こうしゅうさんにょうしょう)は、体内でのシュウ酸(およびその塩)が異常に増加し、尿中に過剰排出されることで知られる遺伝性疾患です。この病気は腎結石や腎不全などの深刻な合併症を引き起こす可能性があり、治療法が求められています。高シュウ酸尿症の中でも特に一次性のものは、遺伝的な要因によって引き起こされ、主に肝臓での代謝異常が関与しています。 高シュウ酸尿症の主な特徴は、体内のシュウ酸産生が増加し、その結果、痛みを伴う尿路結石が生成されることです。この病気は重度の腎障害を引き起こす可能性があるため、早期の診断と治療が重要です。特に、症状が出る前に早期に発見できれば、合併症を防ぐことができるため、患者には定期的な健康診断が勧められています。 現在、高シュウ酸尿症の治療にはいくつかのアプローチがあり、一部の患者にはライフスタイルや食事の管理が求められます。しかし、これだけでは十分な効果が得られないケースも多く、そのための薬物療法が必要となります。一次治療薬としては、最近では新しい薬剤が開発され、臨床での使用が拡大することが期待されています。 高シュウ酸尿症の一次治療薬として知られるのは、特に「オキサレート合成酵素阻害剤(OX2)」や「腸管シュウ酸吸収阻害剤」があります。これらは、シュウ酸の産生や吸収を抑えることで、尿中のシュウ酸濃度を低下させ、合併症を防ぐことを目的としています。これにより、患者の生活の質を改善し、腎機能を保護する役割を果たしています。 オキサレート合成酵素阻害剤は、腎臓や肝臓でのシュウ酸の合成を直接的に抑制する作用があり、これにより体内のシュウ酸濃度をコントロールします。腸管シュウ酸吸収阻害剤は、腸内でのシュウ酸の吸収を抑えることで、尿中へのシュウ酸排出を減少させるメカニズムを持っています。これらの薬剤は、特に腎疾患のリスクが高い患者に対して効果的です。 治療法の進展に伴い、最新の技術やアプローチも導入されています。たとえば、遺伝子治療や細胞治療といった先進的な治療法が研究されており、高シュウ酸尿症の根本的な原因にアプローチすることが可能になると期待されています。また、バイオマーカーの開発が進むことで、病気の進行状況を定量化したり、治療の効果をモニタリングする手段が充実しつつあります。 高シュウ酸尿症の治療においては、医師や患者の連携が非常に重要です。患者は自らの健康状態について正確に理解し、適切な治療を受けるための情報を医療提供者と共有することが必要です。そのために、定期的なフォローアップやカウンセリングが推奨されます。 結論として、高シュウ酸尿症の一次治療薬は、この疾患に苦しむ患者に対して新たな希望となるものであり、今後の研究がこの分野において更なる発展をもたらすことが期待されます。患者のQOL(Quality of Life)を向上させるための医療技術の進歩を通じて、彼らがより良い生活を営むことができるような環境が整えられています。これからもより多くの研究と、医療の発展が必要とされるでしょう。 |
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