ポンペ病(Pompe Disease):世界の治験レビュー(2015年上半期版)

GlobalDataが発行した調査報告書(GDHC2728CTIDB)
◆英語タイトル:Pompe Disease Global Clinical Trials Review, H1, 2015
◆商品コード:GDHC2728CTIDB
◆発行会社(リサーチ会社):GlobalData
◆発行日:2015年6月16日
◆ページ数:73
◆レポート形式:英語 / PDF
◆納品方法:Eメール
◆調査対象地域:グローバル
◆産業分野:製薬・医療
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当調査レポートでは、世界におけるポンペ病(Pompe Disease) 治療の臨床試験動向について調査・分析し、アジア太平洋/欧州/北米/中南米の主要国における治験件数、段階(フェーズ)別の治験件数、進捗状況別の治験件数、治験目標の達成状況、有望な薬剤、治験関連の最新ニュース、代表的な企業・大学・研究機関における治験概要、代表的な治験のプロファイルなどのデータをまとめてお届けいたします。

・イントロダクション
  - ポンペ病(Pompe Disease)
  - 当レポートの概要
・ポンペ病(Pompe Disease):各地域別治験状況
  - 各国の治験件数及び平均被験者数
   アジア太平洋の主要国における治験件数
   欧州の主要国における治験件数
   北米の主要国における治験件数
   中東・アフリカの主要国における治験件数
   中南米の主要国における治験件数
・G7諸国での治験件数
・G7諸国での治験件数:段階別
・G7諸国での治験件数:進捗状況別
・段階(フェーズ)別の治験件数:進行中の治験(段階別)
・進捗状況別の治験件数
・治験目標の達成状況
・未完了の治験件数
・一定期間に採用された被験者
・スポンサーの種類別治験件数
・有望なスポンサー
・有望な薬剤
・治験のプロファイル
  - 代表的な企業における治験概要
  - 代表的な大学・研究機関における治験概要
・5つの代表的な治験のプロファイル
【レポートの概要】

Pompe Disease Global Clinical Trials Review, H1, 2015

Summary

GlobalData’s clinical trial report, “Pompe Disease Global Clinical Trials Review, H1, 2015″ provides an overview of Pompe Disease clinical trials scenario. This report provides top line data relating to the clinical trials on Pompe Disease. Report includes an overview of trial numbers and their average enrollment in top countries conducted across the globe. The report offers coverage of disease clinical trials by region, country (G7 & E7), phase, trial status, end points status and sponsor type. Report also provides prominent drugs for in-progress trials (based on number of ongoing trials). Global Data Clinical Trial Reports are generated using Global Data’s proprietary database – Pharma eTrack Clinical trials database. Clinical trials are collated from 80+ different clinical trial registries, conferences, journals, news etc across the globe. Clinical trials database undergoes periodic update by dynamic process.

The report enhances the decision making capabilities and helps to create an effective counter strategies to gain competitive advantage.

Note: Certain sections in the report may be removed or altered based on the availability and relevance of data for the indicated disease.

Scope

- The report provides a snapshot of the global clinical trials landscape
- Report provides top level data related to the clinical trials by Region, Country (G7 & E7), Trial Status, Trial Phase, Sponsor Type and End point status
- The report reviews top companies involved and enlists all trials (Trial title, Phase, and Status) pertaining to the company
- The report provides all the unaccomplished trials (Terminated, Suspended and Withdrawn) with reason for unaccomplishment
- The Report provides enrollment trends for the past five years
- Report provides latest news for the past three months

Note: Certain sections in the report may be removed or altered based on the availability and relevance of data for the indicated disease.

Reasons to buy

- Assists in formulating key business strategies with regards to investment
- Helps in identifying prominent locations for conducting clinical trials which saves time and cost
- Provides top level analysis of Global Clinical Trials Market which helps in identifying key business opportunities
- Supports understanding of trials count and enrollment trends by country in global therapeutics market
- Aids in interpreting the success rates of clinical trials by providing a comparative scenario of completed and uncompleted (terminated, suspended or withdrawn) trials
- Facilitates clinical trial assessment of the indication on a global, regional and country level

Note: Certain sections in the report may be removed or altered based on the availability and relevance of data for the indicated disease.

【レポートの目次】

Table of Contents
Table of Contents 2
List of Tables 4
List of Figures 5
Introduction 6
Pompe Disease 6
Report Guidance 6
Clinical Trials by Region 7
Clinical Trials and Average Enrollment by Country 8
Top Five Countries Contributing to Clinical Trials in Asia-Pacific 10
Top Five Countries Contributing to Clinical Trials in Europe 11
Top Countries Contributing to Clinical Trials in North America 12
Top Countries Contributing to Clinical Trials in Middle East and Africa 13
Top Countries Contributing to Clinical Trials in Central and South America 14
Clinical Trials by G7 Countries: Proportion of Pompe Disease to Metabolic Disorders Clinical Trials 15
Clinical Trials by Phase in G7 Countries 16
Clinical Trials in G7 Countries by Trial Status 17
Clinical Trials by E7 Countries: Proportion of Pompe Disease to Metabolic Disorders Clinical Trials 18
Clinical Trials by Phase in E7 Countries 19
Clinical Trials in E7 Countries by Trial Status 20
Clinical Trials by Phase 21
In Progress Trials by Phase 22
Clinical Trials by Trial Status 23
Clinical Trials by End Point Status 24
Unaccomplished Trials of Pompe Disease 25
Subjects Recruited Over a Period of Time 26
Clinical Trials by Sponsor Type 27
Prominent Sponsors 28
Top Companies Participating in Pompe Disease Therapeutics Clinical Trials 29
Prominent Drugs 30
Latest Clinical Trials News on Pompe Disease 31
May 04, 2015: Cortex Pharmaceuticals Announces Publication of Research Results on the Use of Ampakines CX1739 in the Treatment of Respiratory Disorders 31
May 04, 2015: Cortex Pharmaceuticals Announces Publication of Research Results on the Use of Ampakines CX717 in the Treatment of Respiratory Disorders 31
Clinical Trial Profiles 32
Clinical Trial Overview of Top Companies 32
Sanofi 32
Clinical Trial Overview of Sanofi 32
Amicus Therapeutics, Inc. 34
Clinical Trial Overview of Amicus Therapeutics, Inc. 34
BioMarin Pharmaceutical Inc. 35
Clinical Trial Overview of BioMarin Pharmaceutical Inc. 35
EPS Corporation 36
Clinical Trial Overview of EPS Corporation 36
Cortex Pharmaceuticals, Inc. 37
Clinical Trial Overview of Cortex Pharmaceuticals, Inc. 37
Audentes Therapeutics, Inc. 38
Clinical Trial Overview of Audentes Therapeutics, Inc. 38
Alexion Pharmaceuticals, Inc. 39
Clinical Trial Overview of Alexion Pharmaceuticals, Inc. 39
Clinical Trial Overview of Top Institutes / Government 40
University of Florida 40
Clinical Trial Overview of University of Florida 40
Erasmus MC 41
Clinical Trial Overview of Erasmus MC 41
Duke University Medical Center 42
Clinical Trial Overview of Duke University Medical Center 42
National Taiwan University Hospital 43
Clinical Trial Overview of National Taiwan University Hospital 43
Five Key Clinical Profiles 44
Appendix 71
Abbreviations 71
Definitions 71
Research Methodology 72
Secondary Research 72
About GlobalData 73
Contact Us 73
Disclaimer 73
Source 73

List of Tables
Pompe Disease Therapeutics, Global, Clinical Trials by Region, 2015* 7
Pompe Disease Therapeutics, Global, Clinical Trials and Average Enrollment by Top Countries, 2015* 8
Pompe Disease Therapeutics, Global, Clinical Trials In Progress by Top Countries, 2015* 9
Pompe Disease Therapeutics Clinical Trials, Asia-Pacific, Top Five Countries, 2015* 10
Pompe Disease Therapeutics Clinical Trials, Europe, Top Five Countries, 2015* 11
Pompe Disease Therapeutics Clinical Trials, North America, Top Countries, 2015* 12
Pompe Disease Therapeutics Clinical Trials, Middle East and Africa, Top Countries, 2015* 13
Pompe Disease Therapeutics Clinical Trials, Central and South America, Top Countries, 2015* 14
Proportion of Pompe Disease to Metabolic Disorders Clinical Trials, G7 Countries (%), 2015* 15
Pompe Disease Therapeutics, G7 Countries, Clinical Trials by Phase, 2015* 16
Pompe Disease Therapeutics, G7 Countries, Clinical Trials by Trial Status, 2015* 17
Proportion of Pompe Disease to Metabolic Disorders Clinical Trials, E7 Countries (%), 2015* 18
Pompe Disease Therapeutics, E7 Countries, Clinical Trials by Phase, 2015* 19
Pompe Disease Therapeutics, E7 Countries, Clinical Trials by Trial Status, 2015* 20
Pompe Disease Therapeutics, Global, Clinical Trials by Phase, 2015* 21
Pompe Disease Therapeutics, Global, Clinical Trials In Progress by Phase 2015* 22
Pompe Disease Therapeutics, Global, Clinical Trials by Trial Status, 2015* 23
Pompe Disease Therapeutics Clinical Trials, Global, by End Point Status, 2015* 24
Pompe Disease Therapeutics, Global, Terminated Clinical Trials, 2015* 25
Pompe Disease Therapeutics Clinical Trials, Global, Average Enrollment Target Trends, 2010-2014 26
Pompe Disease Therapeutics Market, Global, Clinical Trials by Sponsor Type, 2015* 27
Pompe Disease Therapeutics Clinical Trials, Global, Key Sponsors, 2015* 28
Pompe Disease Therapeutics Clinical Trials, Global, Top Companies by Phase, 2015* 29
Pompe Disease Therapeutics Clinical Trials, Global, Ongoing Clinical Trials by Prominent Drugs, 2015* 30
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by Sanofi, 2015* 32
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by Amicus Therapeutics, Inc., 2015* 34
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by BioMarin Pharmaceutical Inc., 2015* 35
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by EPS Corporation, 2015* 36
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by Cortex Pharmaceuticals, Inc., 2015* 37
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by Audentes Therapeutics, Inc., 2015* 38
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by Alexion Pharmaceuticals, Inc., 2015* 39
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by University of Florida, 2015* 40
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by Erasmus MC, 2015* 41
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by Duke University Medical Center, 2015* 42
Pompe Disease Therapeutics Clinical Trials Market, Global, Clinical Trials by National Taiwan University Hospital, 2015* 43

List of Figures
Pompe Disease Therapeutics, Global, Clinical Trials by Region (%), 2015* 7
Pompe Disease Therapeutics, Global, Clinical Trials and Average Enrollment by Top Countries, 2015* 8
Pompe Disease Therapeutics, Global, Clinical Trials In Progress by Top Countries, 2015* 9
Pompe Disease Therapeutics Clinical Trials, Asia-Pacific, Top Five Countries (%), 2015* 10
Pompe Disease Therapeutics Clinical Trials, Europe, Top Five Countries (%), 2015* 11
Pompe Disease Therapeutics Clinical Trials, North America, Top Countries (%), 2015* 12
Pompe Disease Therapeutics Clinical Trials, Middle East and Africa, Top Countries (%), 2015* 13
Pompe Disease Therapeutics Clinical Trials, Central and South America, Top Countries (%), 2015* 14
Proportion of Pompe Disease to Metabolic Disorders Clinical Trials, G7 Countries (%), 2015* 15
Pompe Disease Therapeutics, G7 Countries, Clinical Trials by Phase, 2015* 16
Pompe Disease Therapeutics, G7 Countries, Clinical Trials by Trial Status, 2015* 17
Proportion of Pompe Disease to Metabolic Disorders Clinical Trials, E7 Countries (%), 2015* 18
Pompe Disease Therapeutics, E7 Countries, Clinical Trials by Phase, 2015* 19
Pompe Disease Therapeutics, E7 Countries, Clinical Trials by Trial Status, 2015* 20
Pompe Disease Therapeutics, Global, Clinical Trials by Phase (%), 2015* 21
Pompe Disease Therapeutics, Global, Clinical Trials In Progress by Phase, 2015* 22
Pompe Disease Therapeutics, Global, Clinical Trials by Trial Status, 2015* 23
Pompe Disease Therapeutics Clinical Trials, Global, Average Enrollment Target Trends, 2010-2014 26
Pompe Disease Therapeutics Market, Global, Clinical Trials by Sponsor Type (%), 2015* 27
Pompe Disease Therapeutics Clinical Trials, Global, Key Sponsors, 2015* 28
Pompe Disease Therapeutics Clinical Trials, Global, Top Companies by Phase, 2015* 29
Pompe Disease Therapeutics Clinical Trials, Global, Ongoing Clinical Trials by Prominent Drugs, 2015* 30
GlobalData Methodology 72

【掲載企業】

Sanofi
Amicus Therapeutics, Inc.
BioMarin Pharmaceutical Inc.
EPS Corporation
Cortex Pharmaceuticals, Inc.
Audentes Therapeutics, Inc.
Alexion Pharmaceuticals, Inc.

【レポートのキーワード】

ポンペ病(Pompe Disease)、治験、臨床試験、治験、治療薬

【免責事項】
http://www.globalresearch.jp/disclaimer

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